A rare disease diagnosis can affect anyone at any time (the majority being children) and can have a significant impact on the quality of life of patients, their families, and caregivers. Alexion, AstraZeneca Rare Disease’s innovation is driven by understanding people living with rare diseases, which fuels all our efforts. We believe that Beacon, as an umbrella organization, helps bring the rare disease community together on topics of relevance to its members, for example in peer mentoring programmes and the Rarely Heard podcasts. Cambridge is a critical hub in the UK helping to ignite change that improves the lives of people living with a rare disease. Beacon is well placed to facilitate these conversations and we are pleased to collaborate with this organization in its commitment to driving change and finding solutions to the unmet needs of the rare disease community.